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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Male
Muscle development
Calcium Channels
BMD
Dystrophy
Muscular Dystrophy
Metabolism
Multi resolution modeling
Cardiomyopathy
Dystrophie Musculaire de Becker BMD
Becker muscular dystrophy
Animal/physiopathology
Invivo
Gene expression
Centronuclear myopathy
Myotendinous junction
Cultured
Homeostasis
Becker BMD muscular dystrophy
Cells
DHPR α1S
Gene modifiers
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Ex-vivo
Muscles/physiopathology
Knockout
Cell Biology
Inhibitors
Liver
Mitochondrial fission
Dystrophine
LncRNA
Dystrophie Musculaire de Duchenne DMD
Gene Expression Regulation/drug effects
Activin Receptors
Human Umbilical Vein Endothelial Cells
LncARN
Génomique
Genomic
Antisense oligonucleotides
Cardiomyopathie
Modificateurs de gènes
Inbred mdx
Immunoglobulin Fc Fragments/pharmacology
Hepatocellular carcinoma
Multi exon skipping
Long noncoding RNA
Duchenne muscular dystrophy DMD
Diseases
Muscle Strength
Morphogenesis
Skeletal muscle
Dystrophie musculaire de Becker
Multiresolution modeling
CaVβs
Long QT
MES
MiARN
Molecular docking
Animals
Delivery
Calcium
NAD+
Autophagy
Myogenesis
Drp1
CTNNB1
DMD
CD38
Humans
L-Type
Base Sequence
Cell homeostasis
Dystrophin-EGFP
Mice
Epigenetics
Duchenne DMD dystrophy
Inbred C57BL
Mdx mouse
Cachexia
Allele‐specific silencing therapy
Molecular Sequence Data
Muscular Atrophy
Energy Metabolism/drug effects
DMO
Muscle Biology
Cell Line
Dystrophin
NNOS
Clinical trials
Exon skipping
Muscular dystrophy
Becker muscular dystrophy BMD
Dystrophin central domain
Muscle
Duchenne muscular dystrophy
CaV subunits
Dynamin 2
LKB1
Hear